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PE2MAX-mediated prime editing restores Galc function and improves neurobehavioral outcomes in Krabbe disease
- Kim, Min Kyoung;
- Seo, Jung Hwa;
- Yoo, Hee Chan;
- Cho, Sung-Rae
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- PE2MAX-mediated prime editing restores Galc function and improves neurobehavioral outcomes in Krabbe disease
- 저자
- Kim, Min Kyoung; Seo, Jung Hwa; Yoo, Hee Chan; Cho, Sung-Rae
- 발행일
- 2025-12
- 유형
- Meeting Abstract
- 권
- 480